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Showing 1–5 of 5 drugs · filtered

EXONDYS 51 (eteplirsen)

DUCHENNE MUSCULAR DYSTROPHY-EXON SKIPPING ANTISENSE OLIGONUC · DUCHENNE MUSCULAR DYSTROPHY DUE TO GENETIC MUTATION AMENABLE TO EXON 51 SKIPPING THERAPY
SAREPTA THERAPE

VYONDYS-53 (golodirsen)

DUCHENNE MUSCULAR DYSTROPHY-EXON SKIPPING ANTISENSE OLIGONUC · DUCHENNE MUSCULAR DYSTROPHY DUE TO GENETIC MUTATION AMENABLE TO EXON 53 SKIPPING THERAPY
SAREPTA THERAPE

VILTEPSO (viltolarsen)

DUCHENNE MUSCULAR DYSTROPHY-EXON SKIPPING ANTISENSE OLIGONUC · DUCHENNE MUSCULAR DYSTROPHY DUE TO GENETIC MUTATION AMENABLE TO EXON 53 SKIPPING THERAPY
NS PHARMA, INC.

EXONDYS-51 (eteplirsen)

DUCHENNE MUSCULAR DYSTROPHY-EXON SKIPPING ANTISENSE OLIGONUC · DUCHENNE MUSCULAR DYSTROPHY DUE TO GENETIC MUTATION AMENABLE TO EXON 51 SKIPPING THERAPY
SAREPTA THERAPE

AMONDYS-45 (casimersen)

DUCHENNE MUSCULAR DYSTROPHY-EXON SKIPPING ANTISENSE OLIGONUC · DUCHENNE MUSCULAR DYSTROPHY DUE TO GENETIC MUTATION AMENABLE TO EXON 45 SKIPPING THERAPY
SAREPTA THERAPE